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Recruiting
NCT NCT07223203
TRITON-PN: A Study to Evaluate the Efficacy and Safety of Nucresiran in Patients With Hereditary Transthyretin Amyloidosis With Polyneuropathy
Not yet reported
Alnylam Pharmaceuticals
125 participants
Est. completion 2031-06-12
56 sites
Other conditions: Hereditary Transthyretin-Mediated Amyloidosis With Polyneuropathy, hATTR-PN
View official trial listing →
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Completed
NCT NCT02797847
A Safety and Tolerability Study of an Investigational Drug, ALN-TTRSC02, in Healthy Subjects
Not yet reported
Alnylam Pharmaceuticals
80 participants
Est. completion 2018-01-12
1 site
Other conditions: Transthyretin-mediated Amyloidosis (ATTR Amyloidosis)
View official trial listing →
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Completed
NCT NCT03759379
HELIOS-A: A Study of Vutrisiran (ALN-TTRSC02) in Patients With Hereditary Transthyretin Amyloidosis (hATTR Amyloidosis)
Not yet reported
Alnylam Pharmaceuticals
164 participants
Est. completion 2025-11-05
64 sites
Stand-alone
Other conditions: Amyloidosis, Hereditary, Transthyretin Amyloidosis
View official trial listing →
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Active, not recruiting
NCT NCT04153149
HELIOS-B: A Study to Evaluate Vutrisiran in Patients With Transthyretin Amyloidosis With Cardiomyopathy
Not yet reported
Alnylam Pharmaceuticals
655 participants
Est. completion 2026-12-02
119 sites
Stand-alone
Other conditions: Transthyretin Amyloidosis (ATTR) With Cardiomyopathy
View official trial listing →
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Completed
NCT NCT05635045
Evuzamitide in PET/CT to Measure Potential Therapeutic Response in ATTR
Not yet reported
Columbia University
10 participants
Est. completion 2024-06-12
1 site
Other conditions: Transthyretin Amyloidosis
View official trial listing →
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Active, not recruiting
NCT NCT05873868
Myocardial Effects in Patients With ATTRv With Polyneuropathy Treated With Patisiran or Vutrisiran
Rennes University Hospital
20 participants
Est. completion 2027-12
5 sites
Other conditions: Transthyretin Amyloidosis, Amyloidosis, Hereditary
View official trial listing →
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Enrolling by invitation
NCT NCT06679946
A Study to Evaluate Vutrisiran in Patients With Transthyretin Amyloidosis With Cardiomyopathy
Not yet reported
Alnylam Pharmaceuticals
700 participants
Est. completion 2028-03-31
87 sites
Stand-alone
Other conditions: Transthyretin Amyloidosis (ATTR) With Cardiomyopathy
View official trial listing →