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Recruiting
NCT NCT05163288
A Pivotal Study of N-Acetyl-L-Leucine on Niemann-Pick Disease Type C
Not yet reported
IntraBio Inc
53 participants
Est. completion 2030-12
14 sites
Stand-alone
Other conditions: Niemann-Pick Disease, Type C
View official trial listing →
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Recruiting
NCT NCT07221292
Pivotal Study of N-acetyl-L-leucine for CACNA1A
Not yet reported
IntraBio Inc
60 participants
Est. completion 2028-11-01
11 sites
Stand-alone
Other conditions: CACNA1A, Spinocerebellar Ataxia Type 6, Episodic Ataxia Type 2, Familial Hemiplegic Migraine-1
View official trial listing →
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Completed
NCT NCT01885338
N-acetylcysteine (NAC) for Improving Cognitive Dysfunction in Schizophrenia
Not yet reported
VA Greater Los Angeles Healthcare System
26 participants
Est. completion 2014-05
1 site
Other conditions: Schizophrenia
View official trial listing →
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Completed
NCT NCT03759639
N-Acetyl-L-Leucine for Niemann-Pick Disease, Type C (NPC)
Not yet reported
IntraBio Inc
33 participants
Est. completion 2022-11-07
9 sites
Stand-alone
Other conditions: Niemann-Pick Disease, Type C
View official trial listing →
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Completed
NCT NCT03759665
N-Acetyl-L-Leucine for GM2 Gangliosidosis (Tay-Sachs and Sandhoff Disease)
Not yet reported
IntraBio Inc
30 participants
Est. completion 2023-01-09
8 sites
Stand-alone
Other conditions: GM2 Gangliosidosis, Tay-Sachs Disease, Sandhoff Disease
View official trial listing →
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Terminated
NCT NCT03759678
N-Acetyl-L-Leucine for Ataxia-Telangiectasia (A-T)
Not yet reported
IntraBio Inc
17 participants
Est. completion 2025-10-27
4 sites
Stand-alone
Other conditions: Ataxia Telangiectasia
View official trial listing →
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Terminated
NCT NCT04784234
Vision Preservation and Restoration Following a 6 Month Trial of GlaucoCetin
Not yet reported
Wills Eye
12 participants
Est. completion 2022-10-27
1 site
Other conditions: Primary Open Angle Glaucoma
View official trial listing →
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Active, not recruiting
NCT NCT06673056
A Pivotal Study of N-Acetyl-L-Leucine on Ataxia-Telangiectasia (A-T)
Not yet reported
IntraBio Inc
60 participants
Est. completion 2028-06-01
11 sites
Stand-alone
Other conditions: Ataxia-Telangiectasia, Ataxia-Telangiectasia (A-T)
View official trial listing →
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Approved For Marketing
NCT NCT07380165
Expanded Access Program (EAP) of Levacetylleucine for Ataxia-Telangiectasia (A-T)
IntraBio Inc
Other conditions: Ataxia-Telangiectasia (A-T)
View official trial listing →