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Recruiting
NCT NCT07054515
A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of Niemann-Pick Type C Disease, GM1 Gangliosidosis or GM2 Gangliosidosis
Not yet reported
Azafaros B.V.
147 participants
Est. completion 2028-06-14
38 sites
Stand-alone
Other conditions: Niemann-Pick Type C Disease, GM1 Gangliosidosis, GM2 Gangliosidosis
View official trial listing →
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Recruiting
NCT NCT07082725
A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of Niemann-Pick Type C Disease (NPC)
Not yet reported
Azafaros B.V.
72 participants
Est. completion 2028-06-14
34 sites
Stand-alone
Other conditions: Niemann-Pick Type C Disease
View official trial listing →
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Recruiting
NCT NCT07399704
A Study to Evaluate the Safety and Efficacy of Nizubaglustat (AZ-3102) in Patients With GM2 Gangliosidosis or Niemann-Pick Type C Disease
Not yet reported
Azafaros B.V.
21 participants
Est. completion 2030-08-07
3 sites
Stand-alone
Other conditions: GM2 Gangliosidosis, Niemann-Pick Type C Disease
View official trial listing →
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Completed
NCT NCT05758922
Phase 2 Study Evaluating the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Oral AZ-3102 in Patients With GM2 Gangliosidosis or Niemann-Pick Type C Disease
Not yet reported
Azafaros B.V.
13 participants
Est. completion 2026-05-05
3 sites
Stand-alone
Other conditions: GM2 Gangliosidosis, Niemann-Pick Disease, Type C
View official trial listing →
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Active, not recruiting
NCT NCT07082543
A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of GM1 Gangliosidosis or GM2 Gangliosidosis
Not yet reported
Azafaros B.V.
75 participants
Est. completion 2028-03-06
26 sites
Stand-alone
Other conditions: Gangliosidoses, GM2, Gangliosidosis, GM1
View official trial listing →
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Not yet recruiting
NCT NCT07715084
Study to Evaluate the Efficacy and Safety of Nizubaglustat (AZ-3102) in Patients With Gaucher Disease Type 3 (GD3)
Not yet reported
Azafaros B.V.
20 participants
Est. completion 2029-07
7 sites
Stand-alone
Other conditions: Gaucher Disease Type 3
View official trial listing →