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Recruiting
NCT NCT04808505
A Study to Evaluate the Safety, Efficacy, PK, PD and Immunogenicity of Cipaglucosidase Alfa/Miglustat in IOPD Subjects Aged 0 to <18
Not yet reported
Amicus Therapeutics
36 participants
Est. completion 2027-07
14 sites
Other conditions: Glycogen Storage Disease Type II Infantile Onset
View official trial listing →
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Recruiting
NCT NCT06121011
A Global Prospective Observational Registry of Patients With Pompe Disease
Amicus Therapeutics
500 participants
Est. completion 2034-12-20
41 sites
Other conditions: Pompe Disease
View official trial listing →
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Completed
NCT NCT02675465
First-In-Human Study to Evaluate Safety, Tolerability, and PK of Intravenous ATB200 Alone and When Co-Administered With Oral AT2221
Not yet reported, Not yet reported
Amicus Therapeutics
29 participants
Est. completion 2024-08-22
19 sites
Stand-alone
Other conditions: Pompe Disease
View official trial listing →
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Completed
NCT NCT03729362
A Study Comparing ATB200/AT2221 With Alglucosidase Alfa/Placebo in Adult Subjects With Late-onset Pompe Disease
Not yet reported
Amicus Therapeutics
125 participants
Est. completion 2021-01-15
73 sites
Other conditions: Pompe Disease (Late-onset)
View official trial listing →
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Available
NCT NCT03865836
Expanded Access for ATB200/AT2221 for the Treatment of Pompe Disease
Amicus Therapeutics
Other conditions: Pompe Disease
View official trial listing →
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Active, not recruiting
NCT NCT03911505
ZIP Study-OL Study of Safety, PK, Efficacy, PD, Immunogenicity of ATB200/AT2221 in Pediatrics Aged 0 to < 18 y.o. w/LOPD
Not yet reported
Amicus Therapeutics
21 participants
Est. completion 2026-06
17 sites
Stand-alone
Other conditions: Pompe Disease (Late-onset)
View official trial listing →
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Completed
NCT NCT04138277
A Study to Assess the Long-term Safety and Efficacy of ATB200/AT2221 in Adult Subjects With Late-Onset Pompe Disease (LOPD)
Not yet reported
Amicus Therapeutics
119 participants
Est. completion 2024-12-31
60 sites
Stand-alone
Other conditions: Pompe Disease (Late-onset)
View official trial listing →
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Available
NCT NCT04327973
Expanded Access for ATB200/AT2221 for the Treatment of IOPD
Amicus Therapeutics
4 sites
Other conditions: Pompe Disease Infantile-Onset
View official trial listing →